16 Apr 2015 14:15 - 15:00 Symposium Not recorded Gene Therapy of Hemophilias Amit Nathwani Novel Therapies for Monogenic Diseases 16 Apr 2015 14:15 - 15:00 Share Facebook Linkedin Copy url Audio-visual RSS
Thursday 16 April 2015 Amphithéâtre Maurice Halbwachs, Site Marcelin Berthelot Open to all 14:15 - 15:00 Speaker(s) Amit Nathwani University College, London Events Previous Symposium 16 Apr 2015 09:30 - 10:15 Emmanuelle Charpentier Genome Engineering with CRISPR-Cas9: Biology, Mechanisms and Applicati… Not recorded Symposium 16 Apr 2015 10:15 - 11:00 Alain Fischer Gene Therapy of Primary Immunodeficiencies (PID) Not recorded Symposium 16 Apr 2015 11:00 - 11:45 Luigi Naldini Genetic Engineering of Human Hematopoiesis for the Treatment of Inheri… Not recorded Symposium 16 Apr 2015 14:15 - 15:00 Amit Nathwani Gene Therapy of Hemophilias Not recorded Symposium 16 Apr 2015 15:00 - 15:35 Kris de Boeck New Mutation-Specific Pharmacotherapies for Cystic Fibrosis… Not recorded Symposium 16 Apr 2015 15:35 - 15:55 Judith Melki Added Value of New Genomics Technologies in Undiagnosed Patients Who M… Not recorded Symposium 16 Apr 2015 15:55 - 16:30 Vincent des Portes From Promising Clinical Studies to Recent Clinical Trials for the Frag… Not recorded Symposium 16 Apr 2015 17:00 - 17:35 Rebecca Pruss The Discovery and Development of Olesoxime for Spinal Muscular Atrophy… Not recorded Symposium 16 Apr 2015 17:35 - 17:55 Laurence Legeai-Mallet From Gene Identification to Functional Analysis and Treatment of Achon… Not recorded Symposium 16 Apr 2015 17:55 - 18:15 Valerie Cormier-Daire Inhibition of Thromboxane Synthase, a New Mechanism to Increase Bone D… Not recorded Symposium 16 Apr 2015 18:15 - 18:30 Xavier Nissan Selected Oral Communications: Drug Screening on Hutchinson Gilford Pro… Not recorded Symposium 17 Apr 2015 09:00 - 09:45 José-Alain Sahel Novel Approaches for Treatment of Retinal Diseases Not recorded Symposium 17 Apr 2015 09:45 - 10:15 Anna Buj Bello Gene Replacement Therapy for Myotubular Myopathy Not recorded Symposium 17 Apr 2015 10:15 - 10:35 Arnold Munnich REPS1 Is a Novel Gene of Neurodegeneration with Brain Iron Accumulatio… Not recorded Symposium 17 Apr 2015 11:00 - 11:30 Hélène Puccio Efficient AAV Gene Therapy in Cardiac and Neurological Murine Models f… Not recorded Symposium 17 Apr 2015 11:30 - 11:45 William Lostal Selected Oral Communication: High Expression and Therapeutic Efficienc… Not recorded Symposium 17 Apr 2015 11:45 - 12:00 Nathalie Cartier Selected Oral Communication: Gene Therapy for Alzheimer's Disease: The… Not recorded Symposium 17 Apr 2015 12:00 - 12:45 Franck Dufour et Serge Braun Round Table: Can We Afford Cost of Innovative Therapies for Rare Disea… Not recorded Next See also Alain Fischer, chair Experimental medicine Jean-Louis Mandel, chair Human genetics Novel Therapies for Monogenic Diseases
Symposium 16 Apr 2015 09:30 - 10:15 Emmanuelle Charpentier Genome Engineering with CRISPR-Cas9: Biology, Mechanisms and Applicati… Not recorded
Symposium 16 Apr 2015 10:15 - 11:00 Alain Fischer Gene Therapy of Primary Immunodeficiencies (PID) Not recorded
Symposium 16 Apr 2015 11:00 - 11:45 Luigi Naldini Genetic Engineering of Human Hematopoiesis for the Treatment of Inheri… Not recorded
Symposium 16 Apr 2015 15:00 - 15:35 Kris de Boeck New Mutation-Specific Pharmacotherapies for Cystic Fibrosis… Not recorded
Symposium 16 Apr 2015 15:35 - 15:55 Judith Melki Added Value of New Genomics Technologies in Undiagnosed Patients Who M… Not recorded
Symposium 16 Apr 2015 15:55 - 16:30 Vincent des Portes From Promising Clinical Studies to Recent Clinical Trials for the Frag… Not recorded
Symposium 16 Apr 2015 17:00 - 17:35 Rebecca Pruss The Discovery and Development of Olesoxime for Spinal Muscular Atrophy… Not recorded
Symposium 16 Apr 2015 17:35 - 17:55 Laurence Legeai-Mallet From Gene Identification to Functional Analysis and Treatment of Achon… Not recorded
Symposium 16 Apr 2015 17:55 - 18:15 Valerie Cormier-Daire Inhibition of Thromboxane Synthase, a New Mechanism to Increase Bone D… Not recorded
Symposium 16 Apr 2015 18:15 - 18:30 Xavier Nissan Selected Oral Communications: Drug Screening on Hutchinson Gilford Pro… Not recorded
Symposium 17 Apr 2015 09:00 - 09:45 José-Alain Sahel Novel Approaches for Treatment of Retinal Diseases Not recorded
Symposium 17 Apr 2015 09:45 - 10:15 Anna Buj Bello Gene Replacement Therapy for Myotubular Myopathy Not recorded
Symposium 17 Apr 2015 10:15 - 10:35 Arnold Munnich REPS1 Is a Novel Gene of Neurodegeneration with Brain Iron Accumulatio… Not recorded
Symposium 17 Apr 2015 11:00 - 11:30 Hélène Puccio Efficient AAV Gene Therapy in Cardiac and Neurological Murine Models f… Not recorded
Symposium 17 Apr 2015 11:30 - 11:45 William Lostal Selected Oral Communication: High Expression and Therapeutic Efficienc… Not recorded
Symposium 17 Apr 2015 11:45 - 12:00 Nathalie Cartier Selected Oral Communication: Gene Therapy for Alzheimer's Disease: The… Not recorded
Symposium 17 Apr 2015 12:00 - 12:45 Franck Dufour et Serge Braun Round Table: Can We Afford Cost of Innovative Therapies for Rare Disea… Not recorded