16 Apr 2015 2:15 - 3:00pm Symposium Not recorded Gene Therapy of Hemophilias Amit Nathwani Novel Therapies for Monogenic Diseases 16 Apr 2015 2:15 - 3:00pm Share Facebook LinkedIn Bluesky Threads Copy url Audio-visual RSS
Thursday 16 April 2015 Amphithéâtre Maurice Halbwachs, Site Marcelin Berthelot Open to all 14:15 - 15:00 Speaker(s) Amit Nathwani University College, London Events Previous Symposium 16 Apr 2015 9:30 - 10:15am Emmanuelle Charpentier Genome Engineering with CRISPR-Cas9: Biology, Mechanisms and Applicati… Not recorded Symposium 16 Apr 2015 10:15 - 11:00am Alain Fischer Gene Therapy of Primary Immunodeficiencies (PID) Not recorded Symposium 16 Apr 2015 11:00 - 11:45am Luigi Naldini Genetic Engineering of Human Hematopoiesis for the Treatment of Inheri… Not recorded Symposium 16 Apr 2015 2:15 - 3:00pm Amit Nathwani Gene Therapy of Hemophilias Not recorded Symposium 16 Apr 2015 3:00 - 3:35pm Kris de Boeck New Mutation-Specific Pharmacotherapies for Cystic Fibrosis… Not recorded Symposium 16 Apr 2015 3:35 - 3:55pm Judith Melki Added Value of New Genomics Technologies in Undiagnosed Patients Who M… Not recorded Symposium 16 Apr 2015 3:55 - 4:30pm Vincent des Portes From Promising Clinical Studies to Recent Clinical Trials for the Frag… Not recorded Symposium 16 Apr 2015 5:00 - 5:35pm Rebecca Pruss The Discovery and Development of Olesoxime for Spinal Muscular Atrophy… Not recorded Symposium 16 Apr 2015 5:35 - 5:55pm Laurence Legeai-Mallet From Gene Identification to Functional Analysis and Treatment of Achon… Not recorded Symposium 16 Apr 2015 5:55 - 6:15pm Valerie Cormier-Daire Inhibition of Thromboxane Synthase, a New Mechanism to Increase Bone D… Not recorded Symposium 16 Apr 2015 6:15 - 6:30pm Xavier Nissan Selected Oral Communications: Drug Screening on Hutchinson Gilford Pro… Not recorded Symposium 17 Apr 2015 9:00 - 9:45am José-Alain Sahel Novel Approaches for Treatment of Retinal Diseases Not recorded Symposium 17 Apr 2015 9:45 - 10:15am Anna Buj Bello Gene Replacement Therapy for Myotubular Myopathy Not recorded Symposium 17 Apr 2015 10:15 - 10:35am Arnold Munnich REPS1 Is a Novel Gene of Neurodegeneration with Brain Iron Accumulatio… Not recorded Symposium 17 Apr 2015 11:00 - 11:30am Hélène Puccio Efficient AAV Gene Therapy in Cardiac and Neurological Murine Models f… Not recorded Symposium 17 Apr 2015 11:30 - 11:45am William Lostal Selected Oral Communication: High Expression and Therapeutic Efficienc… Not recorded Symposium 17 Apr 2015 11:45am - 12:00pm Nathalie Cartier Selected Oral Communication: Gene Therapy for Alzheimer's Disease: The… Not recorded Symposium 17 Apr 2015 12:00 - 12:45pm Franck Dufour et Serge Braun Round Table: Can We Afford Cost of Innovative Therapies for Rare Disea… Not recorded Next See also Alain Fischer, chair Experimental medicine Jean-Louis Mandel, chair Human genetics Novel Therapies for Monogenic Diseases
Symposium 16 Apr 2015 9:30 - 10:15am Emmanuelle Charpentier Genome Engineering with CRISPR-Cas9: Biology, Mechanisms and Applicati… Not recorded
Symposium 16 Apr 2015 10:15 - 11:00am Alain Fischer Gene Therapy of Primary Immunodeficiencies (PID) Not recorded
Symposium 16 Apr 2015 11:00 - 11:45am Luigi Naldini Genetic Engineering of Human Hematopoiesis for the Treatment of Inheri… Not recorded
Symposium 16 Apr 2015 3:00 - 3:35pm Kris de Boeck New Mutation-Specific Pharmacotherapies for Cystic Fibrosis… Not recorded
Symposium 16 Apr 2015 3:35 - 3:55pm Judith Melki Added Value of New Genomics Technologies in Undiagnosed Patients Who M… Not recorded
Symposium 16 Apr 2015 3:55 - 4:30pm Vincent des Portes From Promising Clinical Studies to Recent Clinical Trials for the Frag… Not recorded
Symposium 16 Apr 2015 5:00 - 5:35pm Rebecca Pruss The Discovery and Development of Olesoxime for Spinal Muscular Atrophy… Not recorded
Symposium 16 Apr 2015 5:35 - 5:55pm Laurence Legeai-Mallet From Gene Identification to Functional Analysis and Treatment of Achon… Not recorded
Symposium 16 Apr 2015 5:55 - 6:15pm Valerie Cormier-Daire Inhibition of Thromboxane Synthase, a New Mechanism to Increase Bone D… Not recorded
Symposium 16 Apr 2015 6:15 - 6:30pm Xavier Nissan Selected Oral Communications: Drug Screening on Hutchinson Gilford Pro… Not recorded
Symposium 17 Apr 2015 9:00 - 9:45am José-Alain Sahel Novel Approaches for Treatment of Retinal Diseases Not recorded
Symposium 17 Apr 2015 9:45 - 10:15am Anna Buj Bello Gene Replacement Therapy for Myotubular Myopathy Not recorded
Symposium 17 Apr 2015 10:15 - 10:35am Arnold Munnich REPS1 Is a Novel Gene of Neurodegeneration with Brain Iron Accumulatio… Not recorded
Symposium 17 Apr 2015 11:00 - 11:30am Hélène Puccio Efficient AAV Gene Therapy in Cardiac and Neurological Murine Models f… Not recorded
Symposium 17 Apr 2015 11:30 - 11:45am William Lostal Selected Oral Communication: High Expression and Therapeutic Efficienc… Not recorded
Symposium 17 Apr 2015 11:45am - 12:00pm Nathalie Cartier Selected Oral Communication: Gene Therapy for Alzheimer's Disease: The… Not recorded
Symposium 17 Apr 2015 12:00 - 12:45pm Franck Dufour et Serge Braun Round Table: Can We Afford Cost of Innovative Therapies for Rare Disea… Not recorded